Archive for August 2026
Quick Note #20: RNA Therapy Used to Treat Two People with SCN2A-DEE
Excerpt Two boys (aged 9 and 14) with severe developmental and epileptic encephalopathy caused by SCN2A variants (SCN2A-DEE) showed meaningful improvements in seizure reduction and neurodevelopmental outcomes after being treated…
Read MoreWhat Families Should Know About the n-Lorem Foundation?
What Families Should Know About the n-Lorem Foundation? Who is n-Lorem? n-Lorem is a US-based nonprofit that designs, develops, and provides antisense oligonucleotides (ASOs) free for life to individuals with…
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